Check out your Company Bowl for anonymous work chats.
This International Women’s Day – and every day!, PTC will challenge the status quo when it comes to gender equality. Our employees raise their hands to celebrate women’s achievements, raise awareness against bias, and take action for equality. International Women’s Day is a global day dedicated to acknowledging the social, economic, cultural and political achievements of women. The day reminds us to work together to establish global gender parity. Marked annually on March 8, International Women’s Day is celebrated in more than 20 countries around the world by our PTC moment makers.
PTC SVP Corporate & Patient Relations Mary Frances Harmon has a few words about our rare disease mission.
For International Angelman Day, PTC’s clinical operations team is feeling blue...but optimistic! Angelman syndrome is a severe neurological development disorder characterized by developmental delays and problems with motor coordination. This rare disease affects an estimated 15,000 people in the United States, and as many as 500,000 worldwide. PTC is working on a gene therapy for the potential treatment of this disorder.
For 12 years, our clinical operations team has worked tirelessly to develop PTC743 (vatiquinone) – an investigational small molecule therapy for the treatment of mitochondrial disease with refractory epilepsy. Currently, PTC is evaluating for a reduction of seizures in patients in four study locations in the United States (including Seattle, Akron and Houston) …and counting. Read more about this global clinical study into the treatment of mitochondrial epilepsy, and meet our team.
Why should Martin Luther King Day find a place in today’s work / life ecosystem? Our diversity and inclusion leader answers with an emphatic challenge: Why should it not? “Look at all the companies that – during the summer of 2020, after the death of George Floyd – developed great works of literature in the form of diversity commitment statements, and launched internal inquiries to find out what (if anything) they are doing to promote equality. What are these actions worth if business leaders fail to observe the day dedicated to a person who gave his life for equality?” Be inspired by this powerful perspective on what Dr. King and his dream mean to today’s working world.
In 2020, PTC launched a Huntington’s Disease Phase 1 clinical trial to study the effects of PTC518 in healthy volunteers. This represents a year of hard work from our HD Innovation Team (the iTeam), and almost a decade of research before that. Learn how biologist Anu Bhattacharyya, Ph.D. and clinical project leader Brian Beers are working together in a race to treat rare disease.
After four years working with the Passaic Academy for Science and Engineering and a recent partnership with Students 2 Science, PTC is delighted to report we’ve encouraged some extraordinary young scientists, witnessed some passionate teaching, and continue to feel great about this and additional opportunities for corporate social responsibility as a compassionate corporate citizen in the great state of New Jersey! Our Chief Culture & Community Officer Martin Rexroad outlines our history supporting some of the middle school science students in Passaic and Newark, NJ public schools.
Happy holidays! This has been a big year for PTC. Not only have we weathered the COVID-19 storm, but we’ve also launched multiple clinical trials (for our Huntington’s disease program, mitochondrial epilepsies, and even coronavirus), hired more than 50 interns as part of our new Talent Pipeline Program, helped to kick-off the first AADC Deficiency Awareness Day, participated in hundreds of virtual life science events around the world, and become a stronger team of compassionate, hard-working rare disease pioneers. Find out more about our company and our mission on our website.
Since 1992, the United Nations has acknowledged December 3rd as International Day of Disabled Persons – or International Day of Persons with Disabilities, International Day of People with Disabilities and World Disability Day. At PTC, we are honored to share testimony from some of our patients and caregivers who live with rare diseases as they explain what it feels like to live with disabilities, too. Says one adult person with Duchenne muscular dystrophy: “I want people to know I can do anything they can, it just takes me longer or I have to do it differently.”
Did you know that the PTC in PTC Therapeutics stands for Post-Transcriptional Control? For our scientists, that refers to the mechanisms used in altering gene expression as a way to treat certain rare diseases. At PTC Therapeutics, we are working on small molecule and gene therapy treatments for rare diseases like mitochondrial disease, Huntington’s disease, Duchenne muscular dystrophy, spinal muscular atrophy (SMA), and aromatic L-amino acid decarboxylase (AADC) deficiency… to name a few. We are also working to treat COVID-19 (coronavirus) through a mechanism of enzyme suppression. Visit our website to learn more about the PTC in PTC Therapeutics.
